STAT· @statnews · X·2026-10-07 17:13· 3 小时前AI 评分21AI 导读外显子跳跃药物是对FDA鼓励罕见病治疗这一目标的一次关键考验。https://trib.al/E4aaOSS正文Exon-skipping drugs present a critical test for the FDA’s goal of encouraging treatments for rare disease. https://trib.al/E4aaOSS来源：STAT · x.com#国际动态#罕见病查看事件全部后续