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BioMarin· @BioMarin · X·· 21 天前精选AI 评分50
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BioMarin宣布在软骨发育不全症儿童中取得新的III期数据,结果发表于NEJM Evidence,并在ESPE2026以迟发口头报告形式展示。公司称这些发现体现其推进骨骼疾病研究、加深对软骨发育不全症这一骨骼发育不良疾病科学理解的持续投入。

推荐理由

BioMarin公布软骨发育不全症III期数据并同步发表于NEJM Evidence,可了解该罕见骨骼疾病的研发进展。

正文

Today we announced new Phase 3 data in children living with hypochondroplasia, which were published in NEJM Evidence and featured in a late-breaking oral presentation at #ESPE2026.

These findings reflect our continued commitment to advancing research in skeletal conditions and deepening scientific understanding of #hypochondroplasia, a form of skeletal dysplasia that can impact growth, physical function and everyday life for children and families.

Learn more: http://ms.spr.ly/6011akPav

来源:BioMarin · x.com