Damian Garde· @damiangarde · X·· 2026-04-08AI 评分22
AI 导读
十年前,这些药物让FDA陷入分裂。如今,它们可能是部分患者最大的希望 https://www.statnews.com/2026/04/08/duchenne-exon-skipping-breakthrough-one-mother-quest/
正文
A decade ago, these drugs tore apart the FDA. Today, they might be some patients’ best hope https://www.statnews.com/2026/04/08/duchenne-exon-skipping-breakthrough-one-mother-quest/
来源:Damian Garde · x.com