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NEJM· Kasiani C. MyersCincinnati Children’s Hospital Medical Center, CincinnatiJean DonadieuSorbonne Université–Hôpital Armand-Trousseau, Assistance Publique–Hôpitaux de Paris, ParisBenjamin GoldbergManon DelafoyBoston Children’s Hospital, BostonCornelia ZeidlerSabine Mellor-HeinekeUniversity of Tubingen, Tubingen, GermanyYang WanXiaofan ZhuInstitute of Hematology and Blood Diseases Hospital, Tianjin, ChinaSimone CesaroMarco CipolliAzienda Ospedaliera Universitaria Integrata Verona, Verona, ItalyKenichiro WatanabeShizuoka Children’s Hospital, Shizuoka, JapanLucy C. FoxMonash University, Melbourne, VIC, AustraliaCaroline RuttenTaco W. KuijpersAmsterdam University Medical Center, AmsterdamAntonis KattamisPolyxeni DelaportaNational and Kapodistrian University of Athens, AthensUlla Wartiovaara-KauttoOuti KilpivaaraHelsinki University Hospital Comprehensive Cancer Center, HelsinkiAlison A. BertuchCandelaria O’FarrellBaylor College of Medicine, HoustonMelanie CotterEoghan DunleaChildren’s Health Ireland, DublinChristopher R. ReillyDana–Farber Cancer Institute, BostonAlan J. WarrenUniversity of Cambridge, Cambridge, United KingdomAmy GeddisSeattle Children’s Hospital, SeattleEdie WellerAkiko Shimamurafor the International SDS Research Consortium*Boston Children’s Hospital, Boston·· 7 天前AI 评分20

Shwachman–Diamond 综合征的累积血液学疾病负担与结局

Cumulative Hematologic Morbidity and Outcomes in Shwachman–Diamond Syndrome

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《NEJM》发表研究,评估 Shwachman–Diamond 综合征患者的累积血液学疾病负担与结局。该文刊于 2026 年 9 月 24 日出版的第 395 卷第 12 期,页码 1241-1244。

来源:NEJM · nejm.org