STAT· @statnews · X·· 4 小时前AI 评分12
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1/ Yannick 和 Brecken 因为相同的诊断而成为朋友。 这两个男孩分别 13 岁和 12 岁,都患有杜氏肌营养不良,一种罕见、致命的肌肉萎缩疾病。 但只有 Brecken 接受了治疗该病的一种有前景的新药。https://bit.ly/3Vz8wM4
正文
1/ Yannick and Brecken became friends because of their diagnosis.
Each boy, age 13 and 12 respectively, has Duchenne muscular dystrophy, a rare, fatal muscle-wasting disease.
But only Brecken has received a promising new drug to treat the condition. https://bit.ly/3Vz8wM4
来源:STAT · x.com