Matthew Herper· @matthewherper · X·· 1 天前精选AI 评分65
AI 导读
STAT 报道，UniQure 的亨廷顿病基因疗法在四年随访中仍在延缓疾病进展。但与一年前的类似分析相比，该疗法获益的幅度有所减弱。报道由 Adam Feuerstein 撰写，原文链接为 https://www.statnews.com/2026/09/29/uniqure-huntingtons-gene-therapy-slows-disease-progression-four-years/。
推荐理由
四年随访数据显示该基因疗法仍在延缓亨廷顿病进展，但获益幅度较一年前分析有所减弱，可供关注长期疗效走势的读者参考。
正文
UniQure’s gene therapy continues to slow Huntington’s progression after four years
But the magnitude of the treatment’s benefit waned compared to a similar analysis from a year ago
By @adamfeuerstein
https://www.statnews.com/2026/09/29/uniqure-huntingtons-gene-therapy-slows-disease-progression-four-years/ via @statnews
来源：Matthew Herper · x.com